Hong Kong pulls visa for man behind gene-edited babies claim
February 21, 2023 GMTBEIJING (AP) — Hong Kong on Tuesday revoked a visa it granted to a Chinese scientist who set off an ethical debate five years ago with claims that he made the world’s first genetically edited babies, pulling it hours after he announced his research plans in the financial hub.
Promising gene therapy delivers treatment directly to brain
January 24, 2023 GMTWhen Rylae-Ann Poulin was a year old, she didn’t crawl or babble like other kids her age. A rare genetic disorder kept her from even lifting her head. Her parents took turns holding her upright at night just so she could breathe comfortably and sleep.
$3.5M gene therapy for hemophilia gets FDA approval
November 22, 2022 GMTWASHINGTON (AP) — U.S. health regulators on Tuesday approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder.
The Food and Drug Administration cleared Hemgenix, an IV treatment for adults with hemophilia B, the less common form of the genetic disorder which primarily affects men.
Death in US gene therapy study sparks search for answers
November 4, 2022 GMTThe lone volunteer in a unique study involving a gene-editing technique has died, and those behind the trial are now trying to figure out what killed him.
Terry Horgan, a 27-year-old who had Duchenne muscular dystrophy, died last month, according to Cure Rare Disease, a Connecticut-based nonprofit founded by his brother, Rich, to try and save him from the fatal condition.
Doctors: Cancer patients cured a decade after gene therapy
February 2, 2022 GMTIn 2010, doctors treated Doug Olson’s leukemia with an experimental gene therapy that transformed some of his blood cells into cancer killers. More than a decade later, there's no sign of cancer in his body.
PerkinElmer to pay $5.25B for antibody maker BioLegend
July 26, 2021 GMTPerkinElmer will spend about $5.25 billion to acquire BioLegend, which makes antibodies used in gene therapy and reagents for drug discovery.
The Waltham, Massachusetts, company said Monday that it will pay a combination of cash and stock for the privately held BioLegend in a deal expected to close by the end of the year.
Newer methods may boost gene therapy’s use for more diseases
June 2, 2021 GMTJordan Janz knew his gamble on an experimental gene therapy for his rare disease might be paying off when he returned to work and a friend sniffed him.
“He said, ‘you have a normal smell, you smell good,’” Janz recalled.
AIDS virus used in gene therapy to fix ‘bubble baby’ disease
May 11, 2021 GMTA gene therapy that makes use of an unlikely helper, the AIDS virus, gave a working immune system to 48 babies and toddlers who were born without one, doctors reported Tuesday.
Results show that all but two of the 50 children who were given the experimental therapy in a study now have healthy germ-fighting abilities...
Former St. Jude Children’s Research Hospital director dies
February 9, 2021 GMTMEMPHIS, Tenn. (AP) — Dr. Arthur W. Nienhuis, a former director of St. Jude Children's Research Hospital in Memphis, Tennessee, has died, the hospital said.
Nienhuis died Feb. 3, the hospital said in a statement released Monday.
Lilly lays out 2021 expectations, gene therapy acquisition
December 15, 2020 GMTShares of Eli Lilly climbed Tuesday after the drugmaker laid out a better-than-expected revenue forecast and plans to buy a young company developing a potential Parkinson’s disease treatment...
Egan-Jones Recommends Against Electing Dissident’s Full Slate of Nominees to Ziopharm Board
December 11, 2020 GMT
Recommends
A
gainst
E
lecting
WaterMill Nominee
Jaime Vieser
Ziopharm Continues to Recommend that Shareholders Support Company’s Strong Progress by Return ing the GREEN Consent Revocation Card
Germany’s Bayer to buy US gene therapy specialist AskBio
October 26, 2020 GMTBERLIN (AP) — German health care company Bayer said Monday it is buying Asklepios BioPharmaceutical, a U...
Genprex and University of Pittsburgh Sign Exclusive License Agreement for Potentially Curative Gene Therapy Candidate for Diabetes
February 11, 2020 GMTAUSTIN, Texas & CAMBRIDGE, Mass.--(BUSINESS WIRE)--Feb 11, 2020--
New, old drugs may offer fresh ways to fight heart disease
November 18, 2019 GMTPHILADELPHIA (AP) — Novel drugs may offer fresh ways to reduce heart risks beyond the usual medicines to lower cholesterol and blood pressure...
FDA says Novartis withheld data problem before drug approval
August 6, 2019 GMTTRENTON, N.J. (AP) — U.S. regulators want to know why Novartis didn't disclose a problem with testing data until after the Swiss drugmaker's $2...
At $2M, priciest ever medicine treats fatal genetic disease
May 24, 2019 GMTU.S. regulators have approved the most expensive medicine ever, for a rare disorder that destroys a baby's muscle control and kills nearly all of those with the most common type of the disease within a couple of years...
Doctors use HIV in gene therapy to fix ‘bubble boy’ disease
April 17, 2019 GMTThey were born without a working germ-fighting system, every infection a threat to their lives. Now eight babies with "bubble boy disease" have had it fixed by a gene therapy made from one of the immune system's worst enemies — HIV, the virus that causes AIDS...
Officials remove special rules for gene therapy experiments
August 15, 2018 GMTU.S. health officials are eliminating special regulations for gene therapy experiments, saying that what was once exotic science is quickly becoming an established form of medical care with no extraordinary risks...
Pharma BI joins forces against cystic fibrosis
August 7, 2018 GMTBoehringer Ingelheim is upping its game in the fight against cystic fibrosis and jumping into the gene therapy realm.
The pharmaceutical company with U.S. headquarters in Ridgefield announced this week a partnership with the UK Cystic Fibrosis Gene Consortium, Imperial Innovations and Oxford BioMedica.
Can gene therapy be harnessed to fight AIDS virus?
March 1, 2018 GMTCan gene therapy be harnessed to fight the AIDS virus?
February 13, 2018 GMTFor more than a decade, the strongest AIDS drugs could not fully control Matt Chappell's HIV infection. Now his body controls it by itself, and researchers are trying to perfect the gene editing that made this possible.
2nd man has gene editing; therapy has no safety flags so far
February 7, 2018 GMTA second patient has been treated in a historic gene editing study in California, and no major side effects or safety issues have emerged from the first man's treatment nearly three months ago, doctors revealed Tuesday...
Price tag on gene therapy for rare form of blindness: $850,000
January 18, 2018 GMTPrice tag on gene therapy for rare form of blindness: $850K
January 3, 2018 GMTWASHINGTON (AP) — A first-of-its kind genetic treatment for blindness will cost $850,000 per patient, making it one of the most expensive medicines in the world and raising questions about the affordability of a coming wave of similar gene-targeting therapies...
In a milestone year, gene therapy finds a place in medicine
December 28, 2017 GMTAfter decades of hope and high promise, this was the year scientists really showed they could doctor DNA to successfully treat diseases...
Gene therapy for rare form of blindness wins US approval
December 19, 2017 GMTWASHINGTON (AP) — U.S. health officials on Tuesday approved the nation's first gene therapy for an inherited disease, a treatment that improves the sight of patients with a rare form of blindness...
Texan with eyesight issues hopes gene therapy helps
December 7, 2017 GMTGene therapy shows promise against blood-clotting disease
December 7, 2017 GMTGene therapy has freed 10 men from nearly all symptoms of hemophilia for a year so far, in a study that fuels hopes that a one-time treatment can give long-lasting help and perhaps even cure the blood disease...
Boy with rare disease gets brand new skin with gene therapy
November 9, 2017 GMTLONDON (AP) — Doctors treating a critically ill boy with a devastating skin disease used experimental gene therapy to create an entirely new skin for most of his body in a desperate attempt to save his life...
US regulators approve 2nd gene therapy for blood cancer
October 19, 2017 GMTTRENTON, N.J. (AP) — U.S. regulators on Wednesday approved a second gene therapy for a blood cancer, a one-time, custom-made treatment for aggressive lymphoma in adults.
The Food and Drug Administration allowed sales of the treatment from Kite Pharma.
Correction: Genetic Frontiers-Blindness-Gene Therapy story
October 10, 2017 GMTIn a story Oct. 9 about an experimental gene therapy for blindness, The Associated Press erroneously reported the deadline for a decision by the U...
US clears breakthrough gene therapy for childhood leukemia
August 30, 2017 GMTWASHINGTON (AP) — Opening a new era in cancer care, U.S. health officials on Wednesday approved a breakthrough treatment that genetically engineers patients' own blood cells into an army of assassins to seek and destroy childhood leukemia...
Novel leukemia treatment could be 1st US gene therapy
July 12, 2017 GMTA treatment for a common childhood blood cancer could become the first gene therapy available in the U...
Swim Across America Greenwich-Stamford set for Saturday
June 22, 2017 GMTGREENWICH — On Saturday, more than 200 swimmers are expected to take part in the 11th annual Swim Across America Greenwich-Stamford Swim, part of a national effort to raise money and awareness in the fight against cancer.
Gene therapy to fight a blood cancer succeeds in major study
February 28, 2017 GMTAn experimental gene therapy that turns a patient's own blood cells into cancer killers worked in a major study, with more than one-third of very sick lymphoma patients showing no sign of disease six months after a single treatment, its maker said Tuesday.